| Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia S Marktel, S Scaramuzza, MP Cicalese, F Giglio, S Galimberti, ... Nature medicine 25 (2), 234-241, 2019 | 223 | 2019 |
| Hematopoietic stem-and progenitor-cell gene therapy for Hurler syndrome B Gentner, F Tucci, S Galimberti, F Fumagalli, M De Pellegrin, P Silvani, ... New England Journal of Medicine 385 (21), 1929-1940, 2021 | 95 | 2021 |
| Preclinical testing of the safety and tolerability of lentiviral vector–mediated above-normal alpha-l-iduronidase expression in murine and human hematopoietic cells using … I Visigalli, S Delai, F Ferro, F Cecere, M Vezzoli, F Sanvito, F Chanut, ... Human gene therapy 27 (10), 813-829, 2016 | 47 | 2016 |
| VISPA: a computational pipeline for the identification and analysis of genomic vector integration sites A Calabria, S Leo, F Benedicenti, D Cesana, G Spinozzi, M Orsini, ... Genome medicine 6, 1-12, 2014 | 34 | 2014 |
| Dactinomycin induces complete remission associated with nucleolar stress response in relapsed/refractory NPM1-mutated AML I Gionfriddo, L Brunetti, F Mezzasoma, F Milano, V Cardinali, R Ranieri, ... Leukemia 35 (9), 2552-2562, 2021 | 28 | 2021 |
| Retrieval of vector integration sites from cell-free DNA D Cesana, A Calabria, L Rudilosso, P Gallina, F Benedicenti, G Spinozzi, ... Nature Medicine 27 (8), 1458-1470, 2021 | 27 | 2021 |
| VISPA2: a scalable pipeline for high-throughput identification and annotation of vector integration sites G Spinozzi, A Calabria, S Brasca, S Beretta, I Merelli, L Milanesi, ... BMC Bioinformatics 18 (1), 520, 2017 | 25 | 2017 |
| GATA1 epigenetic deregulation contributes to the development of AML with NPM1 and FLT3-ITD cooperating mutations P Sportoletti, L Celani, E Varasano, R Rossi, D Sorcini, C Rompietti, ... Leukemia 33 (7), 1827-1832, 2019 | 18 | 2019 |
| adLIMS: a customized open source software that allows bridging clinical and basic molecular research studies A Calabria, G Spinozzi, F Benedicenti, E Tenderini, E Montini BMC bioinformatics 16, 1-11, 2015 | 17 | 2015 |
| ARPIR: automatic RNA-Seq pipelines with interactive report G Spinozzi, V Tini, A Adorni, B Falini, MP Martelli BMC bioinformatics 21, 1-14, 2020 | 15 | 2020 |
| Bcor deficiency perturbs erythro-megakaryopoiesis and cooperates with Dnmt3a loss in acute erythroid leukemia onset in mice P Sportoletti, D Sorcini, AG Guzman, JM Reyes, A Stella, A Marra, ... Leukemia 35 (7), 1949-1963, 2021 | 13 | 2021 |
| Prolonged XPO1 inhibition is essential for optimal antileukemic activity in NPM1-mutated AML G Pianigiani, A Gagliardi, F Mezzasoma, F Rocchio, V Tini, B Bigerna, ... Blood Advances 6 (22), 5938-5949, 2022 | 12 | 2022 |
| Assessing the Impact of Cyclosporin A on Lentiviral Transduction and Preservation of Human Hematopoietic Stem Cells in Clinically Relevant Ex Vivo Gene … C Petrillo, A Calabria, F Piras, A Capotondo, G Spinozzi, I Cuccovillo, ... Human Gene Therapy 30 (9), 1133-1146, 2019 | 11 | 2019 |
| SiCoDEA: a simple, fast and complete app for analyzing the effect of individual drugs and their combinations G Spinozzi, V Tini, A Ferrari, I Gionfriddo, R Ranieri, F Milano, ... Biomolecules 12 (7), 904, 2022 | 9 | 2022 |
| γ-TRIS: a graph-algorithm for comprehensive identification of vector genomic insertion sites A Calabria, S Beretta, I Merelli, G Spinozzi, S Brasca, Y Pirola, ... Bioinformatics 36 (5), 1622-1624, 2020 | 7 | 2020 |
| IL-3-zetakine combined with a CD33 costimulatory receptor as a dual CAR approach for safer and selective targeting of AML VM Perriello, MC Rotiroti, I Pisani, S Galimberti, G Alberti, G Pianigiani, ... Blood Advances 7 (12), 2855-2871, 2023 | 6 | 2023 |
| de Thé, H.; Veal, GJ; Martelli, MP; Falini, B. Dactinomycin Induces Complete Remission Associated with Nucleolar Stress Response in Relapsed/Refractory NPM1-Mutated AML I Gionfriddo, L Brunetti, F Mezzasoma, F Milano, V Cardinali, R Ranieri, ... Leukemia 35 (9), 2552-2562, 2021 | 5 | 2021 |
| ISAnalytics enables longitudinal and high-throughput clonal tracking studies in hematopoietic stem cell gene therapy applications G Pais, G Spinozzi, D Cesana, F Benedicenti, A Albertini, ME Bernardo, ... Briefings in bioinformatics 24 (1), bbac551, 2023 | 3 | 2023 |
| Intrathymic AAV delivery results in therapeutic site-specific integration at TCR loci in mice A Calabria, C Cipriani, G Spinozzi, L Rudilosso, S Esposito, F Benedicenti, ... Blood, The Journal of the American Society of Hematology 141 (19), 2316-2329, 2023 | 2 | 2023 |
| Late phases of hematopoietic reconstitution in metachromatic leukodystrophy gene therapy patients are characterized by lineage commitment of individual HSC clones A Calabria, G Spinozzi, F Benedicenti, D Cesana, L Del Core, E Tenderini, ... MOLECULAR THERAPY 28 (4), 234-234, 2020 | 2 | 2020 |
Andrea CalabriaSan Raffaele Telethon Institute for Gene TherapyEmail verificata su hsr.it
