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Andrea Calabria
Andrea Calabria
San Raffaele Telethon Institute for Gene Therapy
Email verificata su hsr.it
Titolo
Citata da
Citata da
Anno
Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy
A Biffi, E Montini, L Lorioli, M Cesani, F Fumagalli, T Plati, C Baldoli, ...
Science 341 (6148), 1233158, 2013
13402013
Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome
A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ...
Science 341 (6148), 1233151, 2013
12162013
Targeted genome editing in human repopulating haematopoietic stem cells
P Genovese, G Schiroli, G Escobar, T Di Tomaso, C Firrito, A Calabria, ...
Nature 510 (7504), 235-240, 2014
6882014
Targeted genome editing in human repopulating haematopoietic stem cells
P Genovese, G Schiroli, G Escobar, T Di Tomaso, C Firrito, A Calabria, ...
Nature 510 (7504), 235-240, 2014
6882014
Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial
M Sessa, L Lorioli, F Fumagalli, S Acquati, D Redaelli, C Baldoli, ...
The Lancet 388 (10043), 476-487, 2016
4722016
MYO1E mutations and childhood familial focal segmental glomerulosclerosis
C Mele, P Iatropoulos, R Donadelli, A Calabria, R Maranta, P Cassis, ...
New England Journal of Medicine 365 (4), 295-306, 2011
2932011
Precise gene editing preserves hematopoietic stem cell function following transient p53-mediated DNA damage response
G Schiroli, A Conti, S Ferrari, L Della Volpe, A Jacob, L Albano, S Beretta, ...
Cell stem cell 24 (4), 551-565. e8, 2019
2572019
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia
S Marktel, S Scaramuzza, MP Cicalese, F Giglio, S Galimberti, ...
Nature medicine 25 (2), 234-241, 2019
2232019
Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in …
E Salvi, Z Kutalik, N Glorioso, P Benaglio, F Frau, T Kuznetsova, H Arima, ...
Hypertension 59 (2), 248-255, 2012
1812012
Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in …
E Salvi, Z Kutalik, N Glorioso, P Benaglio, F Frau, T Kuznetsova, H Arima, ...
Hypertension 59 (2), 248-255, 2012
1812012
In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells
L Biasco, S Scala, L Basso Ricci, F Dionisio, C Baricordi, A Calabria, ...
Science translational medicine 7 (273), 273ra13-273ra13, 2015
1792015
Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene
L Volpi, G Roversi, EA Colombo, N Leijsten, D Concolino, A Calabria, ...
The American Journal of Human Genetics 86 (1), 72-76, 2010
1562010
Sleeping Beauty–engineered CAR T cells achieve antileukemic activity without severe toxicities
CF Magnani, G Gaipa, F Lussana, D Belotti, G Gritti, S Napolitano, ...
The Journal of clinical investigation 130 (11), 6021-6033, 2020
1202020
A multilevel data integration resource for breast cancer study
E Mosca, R Alfieri, I Merelli, F Viti, A Calabria, L Milanesi
BMC systems biology 4, 1-11, 2010
1182010
HIV-1-mediated insertional activation of STAT5B and BACH2 trigger viral reservoir in T regulatory cells
D Cesana, FR Santoni de Sio, L Rudilosso, P Gallina, A Calabria, ...
Nature communications 8 (1), 498, 2017
992017
Hematopoietic stem-and progenitor-cell gene therapy for Hurler syndrome
B Gentner, F Tucci, S Galimberti, F Fumagalli, M De Pellegrin, P Silvani, ...
New England Journal of Medicine 385 (21), 1929-1940, 2021
962021
Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates
M Milani, A Annoni, F Moalli, T Liu, D Cesana, A Calabria, S Bartolaccini, ...
Science translational medicine 11 (493), eaav7325, 2019
802019
AAV integration in human hepatocytes
DA Dalwadi, A Calabria, A Tiyaboonchai, J Posey, WE Naugler, E Montini, ...
Molecular Therapy 29 (10), 2898-2909, 2021
752021
miRNA-126 orchestrates an oncogenic program in B cell precursor acute lymphoblastic leukemia
S Nucera, A Giustacchini, F Boccalatte, A Calabria, C Fanciullo, T Plati, ...
Cancer cell 29 (6), 905-921, 2016
692016
Safe and efficient gene therapy for pyruvate kinase deficiency
M Garcia-Gomez, A Calabria, M Garcia-Bravo, F Benedicenti, P Kosinski, ...
Molecular Therapy 24 (7), 1187-1198, 2016
652016
Il sistema al momento non può eseguire l'operazione. Riprova più tardi.
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